PTC Therapeutics, Inc.

Clinical Liaison

• Engage with the rare disease community, including patient advocacy organizations, to understand the rare experience and incorporate insights throughout PTC Therapeutics
• Collaborate with internal PTC teams to identify, educate, build, and leverage relationships with people living with rare diseases, caregivers, and Patient Advocacy Organizations
• Assist communities with resources to help remove access barriers and gain coverage for marketed products, when appropriate
• Build patient advocacy and community relationships for currently marketed product disease states and products in development, consistent with applicable regulations
• Work cross-functionally with medical, communications, commercial, legal, and compliance colleagues to follow country-specific guidelines, standards, and regulations
• Connect families to Patient Advocacy Organizations and resources
• Develop, plan, and execute educational programs for people living with rare diseases and their caregivers
• Support Patient Advocacy Organizations through shared interests in education and programs
• Work with the rare disease community to advocate for access to care and therapies

Patient Engagement Liaison – Clinical

Manager

• Provide personalized assistance to patients/caregivers with complex and rare medical conditions
• Work directly with patients/caregivers to help them obtain access to PTC products
• Build relationships with patients, caregivers, HCPs, patient engagement, and the sales team to collect/share information and coordinate patient care
• Solve problems urgently to help patients/caregivers gain access to therapy and maintain adherence
• Communicate with internal and external stakeholders while maintaining confidentiality of patient health information and complying with laws and regulations
• Navigate the CRM system and learn internal business rules and processes
• Report Adverse Events and Product Quality Complaints
• Adhere to PTC’s Standard Operating Procedures and Business Rules
• Interpret patient insurance, prescription, and other health-related documentation
• Handle all aspects of patient cases and complete follow-up promptly and professionally
• Perform clerical and administrative functions such as mailing and faxing
• Maintain subject matter expertise in orphan/rare disease, including conditions, treatments, patient/caregiver communities, and activities/events
• Apply subject matter expertise to drive positive patient outcomes
• Report to the Sr Mgr, Patient Services
• Domestic travel up to 10%

Case Manager, Patient Services

Medical Science Liaison

• Serve as a field-based Medical Science Liaison within Medical Affairs
• Support and represent PTC and its products with KOLs, clinicians, academic institutions, and professional organizations
• Respond to unsolicited requests for information about PTC marketed and developing products
• Build long-term relationships and establish rapport with clinicians through scientific product and disease-state discussions
• Provide medical and clinical expertise on company products and support safe and effective product utilization
• Attend national and regional medical meetings and symposia; engage attendees, attend scientific sessions, gather information, and summarize findings
• Deliver fair-balanced, objective clinical and scientific presentations to HCPs, payors, and patient organizations
• Identify speakers for advisory boards, symposia, and educational programs
• Support regional medical initiatives such as advisory boards
• Provide management with input on competitive therapies, business development opportunities and risks, and market insights
• Establish and maintain relationships with health authorities, KOLs, HCPs, academic institutions, payors, and patient organizations
• Facilitate submissions for unrestricted educational grants and research initiatives
• Maintain awareness of medical/clinical, regulatory, compliance, and quality requirements and support company SOPs
• Maintain and analyze competitor information and communicate relevant intelligence to internal stakeholders
• Work cross-functionally with internal departments and external resources on Medical Affairs issues

Patient Engagement Liaison – Clinical

Case Manager, Patient Services

Medical Science Liaison – Metabolic